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BioMarin Pharmaceutical Inc., a biotechnology company, engages in the development and commercialization of therapies for life-threatening rare diseases and medical conditions in the United States, Europe, Latin America, the Middle East, the Asia Pacific, and internationally. The company’s products include VIMIZIM, an enzyme replacement therapy for the treatment of mucopolysaccharidosis (MPS) IV type A, a lysosomal storage disorder; VOXZOGO, a once daily injection analog of c-type natriuretic peptide (CNP) for the treatment of achondroplasia; NAGLAZYME, a recombinant form of N- acetylgalactosamine 4-sulfatase for patients with MPS VI; and PALYNZIQ, a PEGylated recombinant phenylalanine (Phe) ammonia lyase enzyme delivered through subcutaneous injection to reduce blood Phe concentrations. It also develops BRINEURA, a recombinant human tripeptidyl peptidase 1 for the treatment of patients with ceroid lipofuscinosis type 2, a form of Batten disease; ALDURAZYME, a purified protein designed to be identical to a naturally occurring form of the human enzyme alpha-L-iduronidase; and KUVAN, a proprietary synthetic oral form of 6R-BH4 that is used to treat patients with phenylketonuria, an inherited metabolic disease. The company’s products under development include BMN 333, a longer-acting CNP for the treatment of multiple growth disorders, such as achondroplasia and hypochondroplasia; and BMN 351, an oligonucleotide for the treatment of duchenne muscular dystrophy. It serves specialty pharmacies, hospitals, non-U.S. government agencies, distributors, and pharmaceutical wholesalers. The company has license and collaboration agreements with and Ares Trading S.A. The company was incorporated in 1996 and is based in San Rafael, California.
Market Challenges | Analyst targets range from $70 to $115, reflecting varied views on BioMarin's ability to navigate increasing competition and maintain market dominance |
Pipeline Potential | Delve into BioMarin's promising pipeline, including BMN333 for achondroplasia and BMN351 for DMD, poised to drive future growth and market expansion |
Financial Strength | Explore BioMarin's robust Q1 2025 results, with $734M in product revenues and projected 9-12% YoY growth, underpinned by a perfect Piotroski Score |
Rare Disease Pionee | BioMarin leads in orphan drug market with innovative therapies, boasting an impressive 81.8% gross margin and stable stock performance |

Metrics to compare | BMRN | Sector Sector - Average of metrics from a broad group of related Healthcare sector companies | Relationship RelationshipBMRNPeersSector | |
|---|---|---|---|---|
P/E Ratio | 30.5x | 18.4x | −0.5x | |
PEG Ratio | −1.67 | −0.68 | 0.00 | |
Price / Book | 1.7x | 2.2x | 2.6x | |
Price / LTM Sales | 3.3x | 2.3x | 3.2x | |
Upside (Analyst Target) | 70.1% | 19.0% | 45.7% | |
Fair Value Upside | Unlock | 50.3% | 4.8% | Unlock |